ACMG, NSGC, and others in the genetics community are monitoring whether the widely used online clinical genetics database ...

NEW YORK – The UK's National Institute for Health and Care Excellence (NICE) on Friday recommended that the National Health Service make AstraZeneca's AKT pathway inhibitor Truqap (capivasertib) with ...

The 2018 accelerated approval of Vitrakvi was converted to full approval based on results from three trials in adult and pediatric patients.

The company expects early cohort data this year from the trial assessing the calpain-2-targeted antisense oligonucleotide therapy.

On the heels of its acquisition by Ocuphire Pharma, Opus is planning next steps for its Leber congenital amaurosis type 5 ...

The FDA cleared the firm this week to begin a Phase I study of ALX2004 in EGFR-expressing solid tumors, which could start in a few months.

Cardinal is using its own cyclotron installations to produce Gozellix for distribution across a range of US locations.

BrainStorm has attempted to gain market approval for NurOwn without success but remains committed to developing the cell therapy.

The recommendation was based on results from the Phase III THOR trial, which compared Balversa to chemotherapy.

With an arsenal of antibody assets based on IgE, IgA, and IgG, the newly combined company has opportunities across cancer indications.

The biotech firm closed an oversubscribed Series C funding round, proceeds from which it will use to advance ATSN-201 and its ...

The new approval makes the regimen an option for around 4,000 patients in the EU who have at least one non-class I CFTR mutation.